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Articles by John

PatientsLikeMe

PatientsLikeMe and Shire to co-develop rare disease patient network

May 9, 2017 John 0

PatientsLikeMe and Shire are to work together to better understand rare disease patient health and disease progression. PatientsLikeMe is now a well-established online community of […]

Gene Therapy

A New Gene Therapy Cure Just Treated Its First-Ever Patient

May 9, 2017 John 0

Rarefied Cures This March, a child with severe combined immune deficiency (SCID) became the second commercial gene therapy patient ever. The patient started receiving a drug […]

Pharma Prices

Big Pharma Losing Leverage as Payers Raise Pressure on Price

May 7, 2017 John 0

Consolidation among insurers, pharmacy benefit managers key Drug companies are citing growth by volume instead of price Byline: Jared S. Hopkins and Doni Bloomfield, Bloomberg […]

NLRP12.com’s 2017 Scottish Council Manifesto released

May 7, 2017 John 0

For the 2017 Scottish Local Council Elections NLRP12.com have released their manifesto for council candidates throughout Scotland. We had hoped to be able to get […]

ICMR-registry-rare-disease

ICMR launches registry of rare diseases

May 6, 2017 John 0

Launched on April 27 by the Indian Council of Medical Research (ICMR), the registry is important for determining the precise number of patients, age of […]

Dr Scott Canna

In a Heartbeat: Understanding autoinflammation (Pittsburgh)

May 6, 2017 John 0

Children’s Hospital of Pittsburgh of UPMC has recruited Dr. Scott Canna to research autoinflammatory disorders, which can cause the body’s immune system to attack its […]

immunity

Researchers Unlock An Immunity ‘Black Box’

May 6, 2017 John 0

A research team led by St. Jude Children’s Research Hospital immunologists has revealed a previously unknown immune machinery that goes awry to trigger the inflammatory […]

NHS ENGLAND NICE

Pharma warns new NICE rules will delay access to meds

May 6, 2017 John 0

Pharma companies are warning that changes to the way the National Institute for Health & Care Excellence (NICE) and NHS England (NHSE) assess new medicines, […]

Prices of Drugs Rare Disease

Ultra-rare disease drugs: has access in England just got harder?

May 6, 2017 John 0

Story from Andrew McConaghie on PharmaPhorum New rules on market access introduced by NICE from 1 April will affect most new medicines – but gaining […]

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