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Gene Therapy

A New Gene Therapy Cure Just Treated Its First-Ever Patient

May 9, 2017 John 0

Rarefied Cures This March, a child with severe combined immune deficiency (SCID) became the second commercial gene therapy patient ever. The patient started receiving a drug […]

NLRP12.com’s 2017 Scottish Council Manifesto released

May 7, 2017 John 0

For the 2017 Scottish Local Council Elections NLRP12.com have released their manifesto for council candidates throughout Scotland. We had hoped to be able to get […]

ICMR-registry-rare-disease

ICMR launches registry of rare diseases

May 6, 2017 John 0

Launched on April 27 by the Indian Council of Medical Research (ICMR), the registry is important for determining the precise number of patients, age of […]

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